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AAV Vector Delivery Strategies for Peripheral Nerves

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21:22

Intrathecal Gene Replacement for IGHMBP2-related Conditions

26:36

Genetic Models for CMT

22:01

Targeting SARM1 and Axon Degeneration as a Design-Modifying Strategy for the Treatment of CMT2A

18:11

Announcement of the 2025 Nobel Prize in Physiology or Medicine

21:14

Understanding Clinical Trials

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